AAV9 intracerebroventricular gene therapy improves lifespan, locomotor function and pathology in a mouse model of Niemann–Pick type C1 disease

This is a publication. If there is no link to the publication on this page, you can try the pre-formated search via the search engines listed on this page.

Authors: Michael P Hughes, Dave A Smith, Lauren Morris, Claire Fletcher, Alexandria Colaco, Mylene Huebecker, Julie Tordo, Nuria Palomar, Giulia Massaro, Els Henckaerts, Simon N Waddington, Frances M Platt, Ahad A Rahim

Journal title: Human Molecular Genetics

Journal number: 27/17

Journal publisher: Oxford University Press

Published year: 2018

Published pages: 3079-3098

DOI identifier: 10.1093/hmg/ddy212

ISSN: 0964-6906