Periodic Reporting for period 1 - X-PAND (Exploiting ex vivo expansion and deep multiomics profiling to bring novel, efficient and safer hematopoietic stem cell gene therapies to clinical application)

X-PAND's main objectives are the following: i) Leverage novel and emerging ex vivo HSC expansion protocols to support next-generation genetic engineering of HSC, improving the safety and efficiency of gene editing and allowing to select correctly-engineered HSC and guarantee a...