Periodic Reporting for period 1 - Holo-GT (Custom-designed gene editing of induced epidermal stem cells for gene therapy of genetic diseases of squamous epithelia)

Epidermolysis Bullosa (EB) is a severe genetic skin disease caused by mutations in the adhesion proteins responsible for maintaining the tight connection between the dermis and epidermis. The recessive form of EB, known as the junctional form, has been effectively treated...