Periodic Reporting for period 4 - CRISS (CRISPR Gene Correction for Severe Combined Immunodeficiency Caused by Mutations in Recombination-activating gene 1 and 2 (RAG1 and RAG2))

SCIDs represent a group of severe primary immunodeficiency disorders primarily caused by genetic mutations that disrupt the development of T-cells. SCIDs can also lead to abnormalities in the function and quantities of B-cells and natural killer cells. Without treatment, SCID...