Adeno-associated virus-mediated CASQ2 delivery rescues phenotypic alterations in a patient-specific model of recessive catecholaminergic polymorphic ventricular tachycardia

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Authors: Francesco Lodola; Diego Morone; Marco Denegri; Rossana Bongianino; Hiroko Nakahama; Lucia Rutigliano; Rosanna Gosetti; Giulia Rizzo; Alessandra Vollero; Michelangelo Buonocore; Carlo Napolitano; Gianluigi Condorelli; Gianluigi Condorelli; Silvia G. Priori; Elisa Di Pasquale

Journal title: Cell Death and Disease

Journal number: Volume 7, Issue 106

Journal publisher: Nature Publishing Group

Published year: 2016

Published pages: Article number e2393

DOI identifier: 10.1038/cddis.2016.304

ISSN: 2041-4889