Periodic Reporting for period 1 - IMPROVING-GT (Innovative strategies to increase engraftment of engineered hematopoietic stem cells and bypass genotoxic conditioning, toward the next-generation gene therapy)

The IMPROVING-GT project was centered around the advancement of hematopoietic stem/progenitor cell gene therapy (HSPC-GT), a promising therapeutic approach for treating various genetic diseases. The administration of HSPC-GT involves the ex vivo genetic correction of HSPCs...