Periodic Reporting for period 1 - fight-dm1 (First In class oliGo THerapy for Myotonic Dystrophy type 1 (DM1))

FIGHT-DM1 is a project aimed at developing, ATX-01, a first-in-class oligo therapy for myotonic dystrophy type 1 (DM1). In order to relieve the health-related pains of patients, our project aims to clinically validate our proposed product, ATX-01, as a disruptive...