Periodic Reporting for period 2 - ReviveSTEM (Dissecting and targeting senescence programs to advance Hematopoietic Stem Cell-based gene therapies)

Inherited diseases of blood lineages can be devastating, but gene-editing offers hope for treating them by precisely correcting genetic defects. One promising method involves editing specific genes in hematopoietic stem and progenitor cells (HSPCs), which are cells that can...