Periodic Reporting for period 4 - IEDAT (Intra Erythrocyte Dexamethasone in the treatment of Ataxia Telangiectasia)

Aim of this project is to provide a safe and efficacious treatment (EryDex) of the neurological symptoms to patients affected by Ataxia Telangiectasia (AT), a rare progressively disabling and life-shortening genetic disease; currently no therapy is available on the market. To...